PipelineHuidaGene has multiple R&D pipelines for ophthalmology and neurology.
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01Neurology Diseases
MECP2 Duplication Syndrome (MDS)
Huntington's Disease (HD)
Amyotrophic Lateral Sclerosis (ALS)
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02Ophthalmology Diseases
RPE65 Mutation-Associated Inherited Retinal Dystrophies (RPE65-IRD)
Neovascular Age-related Macular Degeneration (nAMD)
RHO-Associated Retinitis Pigmentosa (RHO-adRP)
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03Neuromuscular Diseases
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HuidaGene Therapeutics to Present at Multiple Key Conferences Highlighting Advances in CRISPR-based TherapiesMar 03,2025
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European Medicines Agency Issues Positive Opinion on HuidaGene's Triple-Designation HG004 Orphan Designation ApplicationJan 08,2025
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HuidaGene Therapeutics Announces Landmark Publication in Nature Neuroscience Highlighting HG204’s Potential as First RNA-editing Therapy for MECP2 Duplication SyndromDec 12,2024
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